Ronnie and Rachael share baby Dean's story with Type 1 infantile GM1 gangliosidosis. About the GM1 Gangliosidosis EL-PFDD The GM1 ...

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GM1 gangliosidosis (GM1) is a rare genetic disorder that progressively damages cells primarily in the brain and spinal cord, ...

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The GM1 Externally-Led Patient-Focused Drug Development Meeting (EL-PFDD) was held on Friday, October 14th as part of the Cure GM1 ...

YouTube-Cure GM1 Foundation

Samiah Al-Zaidy, MD, Vice President of Clinical Development and Lead on the Passage Bio GM1 Gangliosidosis (GM1) Program, gives an overview ...

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David Weinstein, MD, Senior Vice President of Clinical Development at Passage Bio, gives an overview of GM1 gangliosidosis.

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Samiah Al-Zaidy, MD, Vice President of Clinical Development and Lead on the Passage Bio GM1 Gangliosidosis (GM1) Program, discusses the ...

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From Violet's Father: www.curegm1.org/donate Join us for Rare Disease Month as we share our journey with Violet Aurora Sison Law, ...

YouTube-Cure GM1 Foundation

Mark Forman, MD, PhD, Chief Medical Officer at Passage Bio, gives an overview of GM1 gangliosidosis. As Dr. Forman explains, ...

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